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Generation and characterization of a ~F508 cystic fibrosis mouse model
Animal models of cystic fibrosis - Journal of Cystic Fibrosis
Highly Efficient Gene Editing of Cystic Fibrosis Patient-Derived Airway Basal Cells Results in Functional CFTR Correction: Molecular Therapy
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Kcnn4 is a modifier gene of intestinal cystic fibrosis preventing lethality in the Cftr-F508del mouse | Scientific Reports
ΔF508 in cystic fibrosis: willing but not able | Archives of Disease in Childhood
In vivo correction of cystic fibrosis mediated by PNA nanoparticles | Science Advances
Cystic Fibrosis Mouse Models
PDF) Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
IJMS | Free Full-Text | Unravelling the Regions of Mutant F508del-CFTR More Susceptible to the Action of Four Cystic Fibrosis Correctors | HTML
Frontiers | On the Corner of Models and Cure: Gene Editing in Cystic Fibrosis
Generation and characterization of a ~F508 cystic fibrosis mouse model
Towards next generation therapies for cystic fibrosis: Folding, function and pharmacology of CFTR - Journal of Cystic Fibrosis
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
A mouse model for the cystic fibrosis delta F508 mutation. - Abstract - Europe PMC
ΔF508 - an overview | ScienceDirect Topics
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
iPSC-Derived Intestinal Organoids from Cystic Fibrosis Patients Acquire CFTR Activity upon TALEN-Mediated Repair of the p.F508del Mutation: Molecular Therapy - Methods & Clinical Development
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing - ScienceDirect
Generation and characterization of a ~F508 cystic fibrosis mouse model
Generation and characterization of a ~F508 cystic fibrosis mouse model
Frontiers | Bone Cells Differentiation: How CFTR Mutations May Rule the Game of Stem Cells Commitment?
Frontiers | Animal Models in the Pathophysiology of Cystic Fibrosis
Characterization of two rat models of cystic fibrosis—KO and F508del CFTR—Generated by Crispr‐Cas9 - Dreano - 2019 - Animal Models and Experimental Medicine - Wiley Online Library
Rescue of ΔF508-CFTR Trafficking via a GRASP-Dependent Unconventional Secretion Pathway: Cell
Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis | Scientific Reports
Frontiers | Adapting Proteostasis and Autophagy for Controlling the Pathogenesis of Cystic Fibrosis Lung Disease